{"id":2986,"date":"2021-06-08T15:13:06","date_gmt":"2021-06-08T13:13:06","guid":{"rendered":"https:\/\/elainternational.eu\/?p=2986"},"modified":"2023-03-01T08:17:59","modified_gmt":"2023-03-01T07:17:59","slug":"2986","status":"publish","type":"post","link":"https:\/\/old.elainternational.eu\/en\/2021\/06\/08\/2986\/","title":{"rendered":"2021 : A major advancement in the treatment of adrenoleukodystrophy"},"content":{"rendered":"<p><strong>Thanks to ELA massive investment in research on cerebral adrenoleukodystrophy (CALD), the team of Pr. Patrick Aubourg and Dr. Nathalie Cartier published in 2009 the first results of a gene therapy trial on cerebral adrenoleukodystrophy conducted in France. This research was extended internationally by the Bluebird Bio laboratory which conducted the phase 2\/3 study.<\/strong><br \/>\n<strong>On May 21st 2021, the Committee for Medicinal Products for Human Use (CHMP) of the European Medicine Agency (EMA) adopted a positive opinion recommending marketing authorization for the gene therapy as a treatment in cerebral adrenoleukodystrophy, and on July 21st 2021, the European Commission (EC) has granted marketing authorization.<\/strong><br \/>\n<strong>This is an historical advancement in the treatment of adrenoleukodystrophy.<\/strong><\/p>\n<a href=\"https:\/\/elainternational.eu\/wp-content\/uploads\/2021\/06\/CP-bbb_Skysona_Eng.pdf\" class=\"pdfemb-viewer\" style=\"\" data-width=\"max\" data-height=\"max\" data-toolbar=\"top\" data-toolbar-fixed=\"on\">CP-bbb_Skysona_Eng<\/a>\n","protected":false},"excerpt":{"rendered":"<p>Thanks to ELA massive investment in research on cerebral adrenoleukodystrophy (CALD), the team of Pr. Patrick Aubourg and Dr. Nathalie Cartier published in 2009 the first results of a gene therapy trial on cerebral adrenoleukodystrophy conducted in France. This research was extended internationally by the Bluebird Bio laboratory which conducted<span class=\"more-link\"><a href=\"https:\/\/old.elainternational.eu\/en\/2021\/06\/08\/2986\/\">Read More &rarr;<\/a><\/span><\/p>\n","protected":false},"author":1,"featured_media":2994,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"disable_featured_image":false,"footnotes":""},"categories":[46,54],"tags":[],"table_tags":[],"rttpg_featured_image_url":{"full":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2.jpg",770,430,false],"landscape":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2.jpg",770,430,false],"portraits":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2.jpg",770,430,false],"thumbnail":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-150x150.jpg",150,150,true],"medium":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-300x168.jpg",300,168,true],"large":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2.jpg",770,430,false],"1536x1536":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2.jpg",770,430,false],"2048x2048":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2.jpg",770,430,false],"hoot-medium-thumb":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-460x270.jpg",460,270,true],"hoot-preview":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-465x260.jpg",465,260,true],"hoot-large-thumb":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-690x430.jpg",690,430,true],"hoot-preview-large":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-695x388.jpg",695,388,true],"hoot-wide":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-770x425.jpg",770,425,true],"hoot-extra-wide":["https:\/\/old.elainternational.eu\/wp-content\/uploads\/2021\/06\/aubourg2-770x425.jpg",770,425,true]},"rttpg_author":{"display_name":"phonemELAint_19526","author_link":"https:\/\/old.elainternational.eu\/en\/author\/phonemelaint_19526\/"},"rttpg_comment":0,"rttpg_category":"<a href=\"https:\/\/old.elainternational.eu\/en\/category\/france-en\/\" rel=\"category tag\">France<\/a> <a href=\"https:\/\/old.elainternational.eu\/en\/category\/international-en\/\" rel=\"category tag\">International<\/a>","rttpg_excerpt":"Thanks to ELA massive investment in research on cerebral adrenoleukodystrophy (CALD), the team of Pr. Patrick Aubourg and Dr. Nathalie Cartier published in 2009 the first results of a gene therapy trial on cerebral adrenoleukodystrophy conducted in France. This research was extended internationally by the Bluebird Bio laboratory which conductedRead More &rarr;","_links":{"self":[{"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/posts\/2986"}],"collection":[{"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/comments?post=2986"}],"version-history":[{"count":10,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/posts\/2986\/revisions"}],"predecessor-version":[{"id":3045,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/posts\/2986\/revisions\/3045"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/media\/2994"}],"wp:attachment":[{"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/media?parent=2986"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/categories?post=2986"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/tags?post=2986"},{"taxonomy":"table_tags","embeddable":true,"href":"https:\/\/old.elainternational.eu\/en\/wp-json\/wp\/v2\/table_tags?post=2986"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}